Baseline data from the prioritizing utilization and safety of hydroxyurea using precision in Africa (PUSHUP) trial

Authors: Christine Briscoe, Margarida Muhongo Texeira, Eugênia Mateus, Yolanda Aguilera, Wilma Faustino, Arnaldo Patrocinio, Claudia Halumbala, Morena da Costa, Daniel Púcuta, Jeannine Margolis, Roxanne Wood, Amy Webber, Manpreet Kochhar, Lydia Musula, Joshua Tanzer, Patrick McGann

Published: November 3, 2025

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Cost-effectiveness of hydroxyurea for children with sickle cell disease in sub-saharan Africa: A discrete event simulation model to inform policy and government planning

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Development of the sickle cell outcome grading system (SCOGS), a novel classification system for sickle cell disease severity