Qualitative interviews exploring the patient experience of fatigue in individuals with sickle cell disease (SCD), thalassemia, and pyruvate kinase (PK) deficiency

Authors: Biree Andemariam, NinaMaria Badalamenti, Rae Blaylark, Audra Boscoe, Lily Cannon, Ralph Colasanti, Janie Davis, Daniel Ford, Rachael Grace, Holly John, Charles Jonassaint, Sarah Knight, Kevin Kuo, Laurice Levine, Clarisse Lobo, Jake Macey, Susan Morris, Parija Patel, Tamara Schryver, Nirmish Shah, Raffaella Colombatti

Published: November 3, 2025

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Sickle cell disease trials redefined: Toward unified clinical endpoints through international consensus

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Explainable AI-based prediction of chronic kidney disease as a long-term outcome of sickle cell disease in a large, multi-site observational data cohort