Sickle cell disease trials redefined: Toward unified clinical endpoints through international consensus
Authors: Mohamed Yassin, Nirmish Shah, Andrew Campbell, Salam Al-Kindi, Wally Smith, Charles Jonassaint, Miguel Abboud, Raffaella Colombatti, Dipty Jain, Halima Bello-Manga, Mariane de Montalembert, Ana Silva-Pinto, Steven Okoli, Abdelaziz Fahem, Biree Andemariam
Published: November 3, 2025